Nuvamid is a biotechnology company dedicated to addressing the underlying cause of rare diseases, such as sickle cell disease (SCD). Inherent in our pursuit is a deep commitment to the people who are living with these diseases. To them and to their families, we commit to working with a sense of urgency and scientific rigor to discover and develop new medicines.
It is our duty to carefully evaluate the safety and efficacy of any of our potential new medicines, including IMA001. We believe that clinical trials are the best and most appropriate way to do that. The process is a team effort and we will work closely with researchers, physicians, clinical trial site teams, patients and their families to conduct our studies efficiently and effectively. When successful, data from these studies form the basis of regulatory (i.e. FDA, EMA, or similar regulatory agencies) approvals, which ensure the most equitable and sustainable access to medicines for the people who need them.
We know that patients who are living with SCD and their families are counting on us and that every day matters. Given this, we understand that some patients and their families may be interested in accessing our investigational medicines prior to regulatory approval, and outside of the clinical trial setting, through an expanded access program (sometimes referred to as “early access” or “compassionate use”). Nuvamid does not offer programs that allow access to our investigational medicine prior to regulatory approval. For now, participation in a clinical trial is the only way to access our investigational medicines.
More information about Nuvamid’s current clinical trials is available on this website.